Conference Day Two

Conference Day Two

Thursday 27th June 2024

8:30 am Check-In & Coffee

Reviewing One-Time Payment Mechanisms to Address the Misalignment with the Current Pay-for-Service Model to Improve Patient Access

9:20 am Chair’s Opening Remarks

9:30 am Assessing Value- & Cost-effectiveness: How to Compare Novel Cell and Gene Therapies with Current Standards of Care to Improve Decision-Making

  • Amar Kelkar Stem Cell Transplantation Physician, Dana-Farber Cancer Institute

Synopsis

  • Developing a value framework to justify the benefits behind the pricing.
  • Analyzing cost-effectiveness, i.e., balancing the therapy's cost relative to its benefits and outcomes achieved, considering factors like quality-adjusted life years gained
  • How does each particular C&G treatment impact the overall treatment paradigm and economy?

10:00 am Evaluating Global Healthcare Budgeting Structures & Analyzing their Ability to Handle Large One-Time Payments to Better Allocate Funds

  • Manpreet Sidhu Executive Director - Global Health Economics, Outcomes Research & Epidemiology, Ultragenyx

Synopsis

  • What are the traditional valuation methods and payment methods in US and ex-US?
  • Why these methods may not capture the sustained benefits or potential long-term effects adequately, and what are the hurdles to implementation?
  • What should we consider when establishing payment structures based on the value these therapies deliver over the patient’s lifetime rather than a one-time fee, in times of limited/constrained healthcare budgets?

10:30 am Presentation by Red Nucleus

  • Kyle Clifton Senior Director, Market Access & Commercialization Services, Red Nucleus

Synopsis

Session details to be announced

10:40 am Morning Break & Networking

Exploring Reimbursement Strategies for High-Cost Therapies to Promote Standardization & Roll Out Therapies Quicker

11:30 am Evaluating Inpatient Payment Systems to Address Under-Reimbursement Challenges & Enhance Access to Cell Therapies

  • Laura Okpala Executive Director, Head of Reimbursement Policy, Government Affairs, Gilead Sciences

Synopsis

  • Inpatient delivery and profitability: why therapies are not profitable when delivered in the hospital setting
  • Separating the drug from the service: the challenge of underpayment of services and offsetting the loss through the drug price
  • Bundled payments in the inpatient delivery leading to inadequate reimbursement

12:10 pm Fireside Chat: Exploring the Warranty Model for Reimbursement to Mitigate Potential Loss for Seamless Payment Implementation

  • Jesse Lemberger Senior Director US Strategic Pricing, Pfizer
  • David Foell Senior Director, Specialty Channel Operations, Ultragenyx Pharmaceutical Inc

Synopsis

  • Distinguishing the difference between warranties and value-based agreements: what are the pros and cons? What are associated challenges?
  • Evaluating how to implement warranties for cell and gene products
  • Discussing the payer perspective: receptivity of the market and preference over other payment models

1:00 pm Lunch & Networking Break

Exploring Successful Strategies for Launching Therapies in a Dynamic Market by Delving into Early-Stage Commercial Strategy, Market Insights & Regulatory Policy

2:00 pm Launching Therapies into a Volatile Market & Strategies to Overcome Compounding Challenges for Successful Introduction & Market Adaptation for New Products

  • Jie Zhang Global Value & Access, Cell & Gene Independent Expert

Synopsis

  • Recognizing the increasing challenges arising from multiple cell and gene therapies competing for budgets
  • Assessing the cumulative budget impact of these therapies collectively rather than individually
  • Navigating access and pricing challenges in cell therapy beyond haematology indications to unlock new frontiers and explore opportunities for advancement and patient benefit

2:30 pm Examining Strategic Architectures for Global Gene Therapy Access through Insights in Cross-Functional Collaboration & Market Access for Crafting & Implementing Policy Strategies

Synopsis

  • Facilitate a collaborative exchange of perspectives on market access intricacies and regulatory excellence
  • Collaboratively generate actionable strategies for crafting and implementing robust regulatory and reimbursement public policies
  • Engage in a dynamic discussion on the crucial role of cross-functional collaboration in shaping strategic architectures for optimal cell and gene therapy access

3:00 pm Reviewing Compassionate Use Regulations to Understand the Associated Challenges Required for Fast Delivery & Application to Cell & Gene Therapies

  • Matt Feshbach Founder & Chief Executive Officer, AMBROSE Cell Therapy

Synopsis

  • Navigating the required regulations and walking through what they are
  • Dissecting how to get regulatory approval for compassionate use
  • How does the compassionate use apply to the cell and gene field and what are the challenges associated with that?

3:30 pm Chair’s Closing Remarks

End of Cell & Gene Therapy Pricing & Reimbursement Summit